Artur Cideciyan retweeted
Tomas Aleman et al. @ScheieEye @ChildrensPhila @cideciya study Retinal Degeneration Associated With Biallelic RDH12 Variants: Longitudinal Evaluation of Retinal Structure and Visual Function in Pediatric Patients, iovs.arvojournals.org/articl….
Artur Cideciyan retweeted
New research out in @TheLancet demonstrates the safety & efficacy of ATSN-101 gene therapy for improving vision in patients with Leber congenital amaurosis caused by GUCY2D mutations ft. @cideciya & Tomas Aleman (@ScheieEye) tinyurl.com/3rhdk3ux
Artur Cideciyan retweeted
CHRD co-directors Dr. Cideciyan & Dr. Aleman led a gene therapy trial for LCA1, a rare retinal disease, achieving 100x sight improvement sustained for 1 year. The trial focused on ATSN-101, a subretinal gene therapy. #GeneTherapy #PennMedicine #Ophthalmology #Research #Innovation
Artur Cideciyan retweeted
Artur V. Cideciyan @cideciya et al. @ScheieEye describe a treatment strategy with gene editing for late-onset retinal degeneration caused by a founder variant in C1QTNF5.
doi.org/10.1167/iovs.64.15.3…
Excited to get started planning the Phase 1/2 trial for NPHP5 gene therapy
A first-in-human clinical trial to treat NPHP5 Retinal Degeneration, led by Tomas Aleman, MD, Artur Cideciyan, PhD, Gustavo Aguirre, VMD, PhD & William Beltran, DVM, PhD, was selected for the BGTC Clinical Trial Portfolio, announced at @ASGCTherapy annual meeting. @ScheieEye
Will be moving over to Mastodon soon
Artur Cideciyan @cideciya et al @ScheieEye evaluate rod and cone function and outer retinal structure in macular lesions and surrounding extralesional areas of patients with autosomal dominant Best vitelliform macular dystrophy caused by BEST1 mutations
bit.ly/3Ynf7py
That was a cool game. Thank you NYT. I got 5/7 from "You Be the Ump"
✅✅✅⚪️✅✅⚪️
nyti.ms/3SJsFaS
Artur Cideciyan retweeted
Are you 'Excited to share my new paper!'
Harsh truth:
Most people don't care
5 tips on how to tweet about your new paper to get real engagement
@OpenAcademics @PhD_Genie @PhDVoice @AcademicChatter
Artur Cideciyan retweeted
Phase 1/2 study of CEP290 assc. LCA suggests unilateral intravitreal Sepofarsen (anti-sense oligonucleotide) improves light sensitivity in treated eye of 5 patients with light perception vision @cideciya @ScheieEye @ProQR ow.ly/beTj50IbIg2
Looking forward to participating
Retina Conference 2021: have you registered yet? Visit retina.ie and register for free for our Scientific Day, 5th of November. Our wonderful speakers include @edelmurphy2, Bo Chen, Prof @cideciya and more. #Retina21 #conference #Retina21
Ocular theranostics at #ARVO2021 today 3:30pm EDT.
I will present gene-based therapies in patients with CEP290-LCA and in dogs with NPHP5-LCA.
Robert Zawadzki, Jennifer Kang-Mieler, Karl Csaky, Ursula Schmidt-Erfurth, Valeria Cant…lnkd.in/e33Ygsh lnkd.in/e3pmZGt
Night vision in the RP macula – slow progress towards platform-independent measurements. Today at #ARVO2021, please visit poster by Arun Kumar Krishnan, post-doctoral fellow in my lab, describing rod function in retinitis pigmentosa obtained with MP-1S an…lnkd.in/dcSykbu
Artur Cideciyan retweeted
A @PennMedicine patient w/ Leber congenital amaurosis- which causes genetic childhood #blindness- demonstrated sustained improvement of vision 15 mos after 1 interocular injection of #sepofarsen ft. @cideciya, Samuel Jacobson & Joan O'Brien (@ScheieEye) bit.ly/3sYb5nm
Artur Cideciyan retweeted
Post hoc analyses and follow-up of a patient with Leber congenital amaurosis treated with the antisense oligonucleotide sepofarsen indicate sustained improvement of vision 15 months after receiving a single dose of the drug. @cideciya #ASO nature.com/articles/s41591-0…
Artur Cideciyan retweeted
Great result from our Phase 1/2 clinical trial of sepofarsen in CEP290 mediated #LeberCongenitalAmaurosis. We're looking forward to the results from the Phase 2/3 Illuminate trial next year.
#LCA10 #EyeHealth #Ophthalmology #Retina #Optometry #Ophthalmologist #Optometrist
Post hoc analyses and follow-up of a patient with Leber congenital amaurosis treated with the antisense oligonucleotide sepofarsen indicate sustained improvement of vision 15 months after receiving a single dose of the drug. @cideciya #ASO nature.com/articles/s41591-0…
Includes comment by me and our recent work.
Experiment tests a gene-editing therapy for a hereditary blindness disorder. ift.tt/2VTg7nP
Pieces of my interview with NPR journalist Rob Stein included in his report out today on the use of gene editing to try to treat LCA10, a rare blinding disease. Scroll to last three paragraphs to see my comments.
npr.org/sections/health-shot…
Happy to report our latest publication describing an objective outcome measure relevant for gene-based therapies in severe forms of retinal degeneration.
#genetherapy
#lca lnkd.in/esh_6NB
Artur Cideciyan retweeted
ARVO ED @irisrush63 enjoyed a special performance by @NIHdirector Dr. Francis Collins during a farewell event for former @NEI director Dr. Paul Sieving.























